1st South African Gene
causing
retinal blindness discovered
29th
June 2001
Research findings by South African geneticists have resulted in an
international consortium of researchers making a major genetic discovery.
The South African team lead by Professors Raj Ramesar and Jacquie Greenburg
of the Division of Human Genetics at the University of Cape Town, did the
essential work towards identifying the general position of the gene from DNA
samples from dozens of South Africans affected by Retinitis Pigmentosa (RP).
This inherited form of retinal blindness
starts with night blindness and poor contrast vision, leading to tunnel vision
and eventually total blindness. The
collaborative between the UCT research group and UK scientists led to the
identification of the actual gene defect in the laboratory of Dr Chris
Inglehearn, in Leeds (United Kingdom).
The newly described disease-causing gene (RP13) is remarkable in that
every cell in the body uses the protein (PRP8) produced by the gene. However, people with defects in this gene
apparently have only retinal problems.
Hopefully this breakthrough will help
researchers understand the complex mechanisms involved in retinal degeneration
and also create pathways for possible future therapies. It may also help pharmaceutical companies
develop drugs to slow or stop the progression of the visual loss.
Retinal Degenerations, such as RP and Macular
Degeneration affect thousands of South Africans and millions of people
worldwide. The genetic research at the
University of Cape Town is funded by The Retinal Preservation Foundation of
South Africa soon to be renamed Retina South Africa. The British RP Society funds the Leeds work.
National Secretary of the RP Foundation,
Claudette Medefindt (herself affected by a defect in the culprit gene) said
We would like to thank all our sponsors and supporters who have made this
breakthrough possible. Imagine if this
knowledge was available 25 years ago, it could have prevented my passing the
gene mistake to my two sons. Thankfully the sight of their offspring is now
assured. This is true for dozens of young South Africans carrying this
particular gene mutation. The international progress over the last 3 years
offers hope to all South Africans affected by Retinal Blindness.
These finding will be published in the July issue of the International
Journal Human Molecular Genetics.
For more information, please contact: Claudette
Medefindt Cell: 083 306 5262
Alta
Cell: 082 427 8240 Sandy Tel: (011) 622 4904
Fax:
(011) 622 6277
E-Mail: national@rpsa.org.za